Genetic Syndromes & Gene Therapy

Gene therapy focuses on the defective genes that cause hereditary illnesses. Inheriting a defective (mutated) gene can result in a variety of diseases, including cystic fibrosis and haemophilia. It can also make you more susceptible to some malignancies. Gene therapy can be used to either replace a damaged gene with a healthy one or introduce a new gene that can cure or modify the consequences of a disorder.


  • Hereditary illnesses
  • Cystic fibrosis
  • Gene therapy
  • Haemophilia
  • Gene